Gene edited monkeys offer hope for heart disease patients

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Last Posted: Jul 14, 2018

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• FDA Issues Set of Gene Therapy Draft Guidances  
  Global Genes, July 11, 2018
• Gene edited monkeys offer hope for heart disease patients  
  J Kaiser, Science, July 9, 2018
• Are Payers Ready To Address The Financial Challenges Associated With Gene Therapy?  
  Health Affairs Blog, June 28, 2018
• Genetic Therapies for Sickle Cell Disease.  
  Jayavaradhan Rajeswari et al. Pediatric clinics of North America 2018 Jun 65(3) 465-480
• New Treatment for Phenylketonuria (PKU) Clears Brain Fog  
  R Lewis, PLOS Blogs, June 14, 2018
• Sickle Cell Anemia and Its Phenotypes.  
  Williams Thomas N et al. Annual review of genomics and human genetics 2018 Apr
• Twenty-Five Years of Gene Therapy for ADA-SCID: From Bubble Babies to an Approved Drug.  
  Ferrua Francesca et al. Human gene therapy 2017 Nov 28(11) 972-981
• With tantalizing early results, Sarepta’s gene therapy for Duchenne raises hopes for ‘real change’  
  A Feuerstein, StatNews, June 19, 2018
• Gene therapy is saving children’s lives—but screening to discover who needs it is lagging behind  
  E Mullin, Tech Review, May 31, 2018
• Scott Gottlieb Expects the FDA to Approve 40 Gene Therapies by 2022  
  F Holme, Frontline Genomics, June 8, 2018

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