Gene Therapy as a Curative Option for β-Thalassemia

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Last Posted: Apr 20, 2018

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• Gene Therapy as a Curative Option for β-Thalassemia.  
  Biffi Alessandra et al. The New England journal of medicine 2018 04 (16) 1551-1552
• Gene therapy helps patients avoid blood transfusion, study says  
  CNN, Apr 19, 2018
• Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia.  
  Thompson Alexis A et al. The New England journal of medicine 2018 04 (16) 1479-1493
• Contrasting co-inheritance of alpha and beta mutations in delta beta thalassemia and hereditary persistence of fetal hemoglobin: a study from India.  
  Pandey Hareram, et al. Hematology (Amsterdam, Netherlands) 2018 4 1-5
• Natural regulatory mutations elevate the fetal globin gene via disruption of BCL11A or ZBTB7A binding.  
  Martyn Gabriella E et al. Nature genetics 2018 Apr
• Common ?-globin variants modify hematologic and other clinical phenotypes in sickle cell trait and disease.  
  Raffield Laura M, et al. PLoS genetics 2018 3 (3) e1007293

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