Orphanet Journal of Rare Diseases | Home page

Orphanet Journal of Rare Diseases | Home page

OJRD's 10th Anniversary

Please visit our special 10th Anniversary/ Rare Disease Day site, for new publications, blogs, a quiz, and "OJRD Classics", a look at the journal and its advocacy for the voices of rare diseases over the last decade.

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4. RESEARCH

5. Quantifying benefit-risk preferences for new medicines in rare disease patients and caregivers

   T. Morel, S. Aymé, D. Cassiman, S. Simoens, M. Morgan and M. Vandebroek

   Published on: 26 May 2016
6. RESEARCH

   Nation-wide epidemiological study of Japanese patients with rare viral myelopathy using novel registration system (HAM-net)

   Ariella L. G. Coler-Reilly, Naoko Yagishita, Hiroko Suzuki, Tomoo Sato, Natsumi Araya, Eisuke Inoue, Ayako Takata and Yoshihisa Yamano

   Published on: 25 May 2016
7. RESEARCH

   Pharmaceutical expenditure on drugs for rare diseases in Canada: a historical (2007–13) and prospective (2014–18) MIDAS sales data analysis

   Victoria Divino, Mitch DeKoven, Michael Kleinrock, Rolin L. Wade, Tony Kim and Satyin Kaura

   Published on: 21 May 2016
8. RESEARCH

   Pulmonary and pleural lymphatic endothelial cells from pediatric, but not adult, patients with Gorham-Stout disease and generalized lymphatic anomaly, show a high proliferation rate

   Michiko Mori, Michael Dictor, Nicholas Brodszki, Juan Carlos López-Gutiérrez, María Beato, Jonas S. Erjefält and Erik A. Eklund

   Published on: 18 May 2016
9. RESEARCH

   The partnership of patient advocacy groups and clinical investigators in the rare diseases clinical research network

   Peter A. Merkel, Michele Manion, Rashmi Gopal-Srivastava, Stephen Groft, H. A. Jinnah, David Robertson and Jeffrey P. Krischer

   Published on: 18 May 2016

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