The Dilemma of Two Innovative Therapies for Spinal Muscular Atrophy

Main|Search|PHGKB


Last Posted: Nov 04, 2017

---

• The Dilemma of Two Innovative Therapies for Spinal Muscular Atrophy.  
  van der Ploeg Ans T et al. The New England journal of medicine 2017 11 (18) 1786-1787
• Gene therapy’s new hope: A neuron-targeting virus is saving infant lives  
  J Kaiser, Science, Nov 1, 2017
• Two New Ways to Treat A Deadly Disease: Spinal Muscular Atrophy  
  R Lewis, PLOS Blogs, Nov 2, 2017
• Gene-Editing: Interpretation of Current Law and Legal Policy.  
  Kim Na-Kyoung et al. Development & reproduction 2017 Sep 21(3) 343-349
• Gene therapy for inherited retinal and optic nerve degenerations.  
  Moore Nicholas A et al. Expert opinion on biological therapy 2017 Oct 1-13
• Immuno-Oncology - the translational runway for gene therapy.  
  Weß Ludger et al. Human gene therapy 2017 Oct
• Optimizing Treatment for Cerebral Adrenoleukodystrophy in the Era of Gene Therapy.  
  Engelen Marc et al. The New England journal of medicine 2017 Oct (17) 1682-1684
• What Should Gene Therapy Cost?  
  R Lewis, PLOS Blogs, Oct 26, 2017
• Gene Therapy Approaches to Immunodeficiency.  
  Ghosh Sujal et al. Hematology/oncology clinics of North America 2017 Oct 31(5) 823-834
• What Should Gene Therapy Cost?  
  R Lewis, PLOS Blogs, Oct 26, 2017
• F.D.A. Approves Second Gene-Altering Treatment for Cancer  
  D Grady, New York Times, Oct 18, 2017
• FDA Panel Endorses Gene Therapy For A Form Of Childhood Blindness  
  R Stein, NPR, All Things Considered, Oct 12, 2017
• FDA Vote Sets Stage for Gene Therapy’s Future  
  E Mullin, Technology Review, Oct 12, 2017
• FDA Panel Endorses Gene Therapy For A Form Of Childhood Blindness  
  R Stein, NPR, All Things Considered, Oct 12, 2017
• Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy.  
  Eichler Florian et al. The New England journal of medicine 2017 Oct
• In a First, Gene Therapy Halts a Fatal Brain Disease  
  G Kolata, NY Times, Oct 5, 2017

more