Rational Design Meets Real-World Relevance: Pegunigalsidase Alfa in the Treatment of Fabry Disease by CheckRare Staff| Published on: Apr 16, 2026

Rational Design Meets Real-World Relevance: Pegunigalsidase Alfa in the Treatment of Fabry Disease by CheckRare Staff| Published on: Apr 16, 2026 In this expert-led discussion, the faculty examine how advances in rational drug design are translating into meaningful clinical impact, with a particular focus on pegunigalsidase alfa and its emerging role in patient care for Fabry disease. João Gonçalves, PhD (Faculty of Pharmacy, University of Lisbon), Derralynn Hughes, BM BCh (Professor of Experimental Hematology, Lysosomal Disorders Unit, Royal Free London NHS Foundation Trust and University College London), and Eric Wallace, MD (Professor of Medicine, The University of Alabama at Birmingham) come together to discuss the evolving treatment landscape. https://checkrare.com/rational-design-meets-real-world-relevance-pegunigalsidase-alfa-in-the-treatment-of-fabry-disease/