Genome Therapy Could Lead To New Treatment For Life-Threatening Blood Disorders

By Scienmag On Jul 17, 2017

Genome therapy with beneficial natural mutation could lead to new treatment for life-threatening blood disorders

By introducing a beneficial natural mutation into blood cells using the gene-editing technique CRISPR, a UNSW Sydney-led team of scientists has been able to switch on production of foetal haemoglobin – an advance that could eventually lead to a cure for sickle cell anaemia and other blood disorders.