viernes, 11 de septiembre de 2026
Father Pursues Gene Therapy for Sons With Rare Genetic Variations of Duchenne Muscular Dystrophy by Madaline Spencer| Published on: Sep 11, 2026
Father Pursues Gene Therapy for Sons With Rare Genetic Variations of Duchenne Muscular Dystrophy
by Madaline Spencer| Published on: Sep 11, 2026
Tushar Tangsali, father to two sons with Duchenne muscular dystrophy (DMD), discusses how he’s working to develop a gene therapy for a unique genetic variation of DMD for his sons.
https://checkrare.com/father-pursues-gene-therapy-for-sons-with-rare-genetic-variations-of-duchenne-muscular-dystrophy/
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