Gene therapy for neurological disorders: progress and prospects

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Last Posted: Aug 10, 2018

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• Gene therapy for neurological disorders: progress and prospects
  BE Deverman et al, Nature Rev Drug Discovery, AUgust 10, 2018
• An Appalachian odyssey: Hunting for ALS genes along a sprawling family tree
  E Boodman, Stat News, August 5, 2018
• Management guidelines for paediatric patients receiving chimeric antigen receptor T cell therapy.
  Mahadeo Kris M et al. Nature reviews. Clinical oncology 2018 Aug
• Management guidelines for paediatric patients receiving chimeric antigen receptor T cell therapy
  KM Mahadeo et al, Nature Rev Clin Oncology, August 6, 2018
• First Patient Receives Gene Therapy for Rare Liver Disorder 
  U Conn Health, YouTube video, July 26, 2018
• Gene therapy in hemophilia A: a cost-effectiveness analysis.
  Machin Nicoletta et al. Blood advances 2018 Jul 2(14) 1792-1798
• Broad societal debate should inform the use of genome editing in reproduction
  S Griffin, BMJ, July 23, 2018
• One woman’s race to defuse the genetic time bomb in her genes
  A Regalado, Tech Review, July 23, 2018
• FDA Issues Set of Gene Therapy Draft Guidances
  Global Genes, July 11, 2018
• Fetal gene therapy for neurodegenerative disease of infants.
  Massaro Giulia et al. Nature medicine 2018 Jul

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