Breaking barriers in brain gene therapy Researchers are developing new delivery technologies to bring gene therapies to the central nervous system safely and precisely. Written byAlejandra Manjarrez, PhD

Breaking barriers in brain gene therapy Researchers are developing new delivery technologies to bring gene therapies to the central nervous system safely and precisely. Written byAlejandra Manjarrez, PhD https://www.drugdiscoverynews.com/breaking-barriers-in-brain-gene-therapy-17537 By correcting, replacing, or silencing disease-causing genes, gene therapies offer the potential to treat disorders at their source rather than simply managing symptoms. Several gene therapies have already reached the clinic for inherited diseases, demonstrating the promise of genetic medicines. Yet, despite a few landmark approvals for central nervous system (CNS) disorders, widespread and precise delivery to the brain remains one of the field’s greatest challenges.