MicroRNAs in the prognosis and therapy of colorectal cancer: From bench to bedside.

Main|Search|PHGKB

The gene therapy involved inserting a functional copy of the NPC1 gene into mice with the disease. The treated animals were then found to have less severe NPC1 symptoms.NHGRI




Last Posted: Nov 09, 2018

---

• MicroRNAs in the prognosis and therapy of colorectal cancer: From bench to bedside.
  To Kenneth Kw et al. World journal of gastroenterology 2018 Jul 24(27) 2949-2973
• Toward personalized medicine in Bardet-Biedl syndrome.
  Kenny Joanna et al. Personalized medicine 2017 14(5) 447-456
• Thousands of sickle cell and hemophilia patients are waiting for gene therapies. Can manufacturers keep up?
  E Mullin, Stat News, November 5, 2018
• Emerging Genetic Therapy for Sickle Cell Disease.
  Orkin Stuart H et al. Annual review of medicine 2018 Oct
• Genetic screening of Russian Usher syndrome patients toward selection for gene therapy.
  Ivanova Marianna E et al. Ophthalmic genetics 2018 Oct 1-8
• RNAi Rollercoaster Begins to Reap Therapies
  BM Kuehn, JAMA, October 30, 2018
• CRISPR opens door to new type of medicine—'genome surgery'
  A Bleicher, UCSF, October 26, 2018
• Two sick children and a $1.5 million bill: One family’s race for a gene therapy cure
  A Regalado, Tech Review, October 23, 2018
• Promise of Precision Medicine in Psychiatry Nears Reality
  L Davenport, Medscape, October 1o, 2018
• Results of 5-year follow-up study in patients with peripheral artery disease treated with PL-VEGF165 for intermittent claudication.
  Deev Roman et al. Therapeutic advances in cardiovascular disease 2018 Sep 12(9) 237-246

more