Register of designated Orphan Medicinal Products (alphabetical)

New designations June 2011

- Treatment of pancreatic cancer: Salirasib

- Treatment of hepatocellular carcinoma: Sulfonated monophosphorylated mannose oligosaccharide

- Treatment of epidermolysis bullosa: Human dermal fibroblasts cultured on a bioresorbable polyglactin mesh

- Treatment of Stargardt's disease: Human embryonic stem-cell-derived retinal pigment epithelial cells

- Treatment of pouchitis: Metronidazole

- Treatment of 5q spinal muscular atrophy: Viral vector containing DNA encoding the human SMN protein

- Treatment of mucopolysaccharidosis type IIIA (Sanfilippo A syndrome): Adeno-associated viral vector serotype 9 containing the human sulfamidase gene

- Treatment of acute lymphoblastic leukaemia: Allogeneic T cells encoding an exogenous TK gene

- Treatment of neuroblastoma: Chimeric monoclonal antibody against GD2

- Treatment of pancreatic cancer: Genetically modified human adenovirus encoding human PH20 hyaluronidase



▲ All Orphan Drugs in Europe ► Register of designated Orphan Medicinal Products (alphabetical): "- Enviado mediante la barra Google"

▲▲ European Public Assessment Reports (EPARs) ► European Medicines Agency - European public assessment reports - European public assessment reports: "- Enviado mediante la barra Google"

open here please:
Register of designated Orphan Medicinal Products (alphabetical): "- Enviado mediante la barra Google"