miércoles, 27 de mayo de 2026

Itvisma Gene Therapy for Patients With Spinal Muscular Atrophy by CheckRare Staff| Published on: May 27, 2026

Itvisma Gene Therapy for Patients With Spinal Muscular Atrophy by CheckRare Staff| Published on: May 27, 2026 John Day, MD, PhD, Director of Neuromuscular Medicine at Stanford University, discusses the development of Itvisma gene therapy for patients with spinal muscular atrophy (SMA). https://checkrare.com/itvisma-gene-therapy-for-patients-with-spinal-muscular-atrophy/

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