Breaking the bottlenecks: How a more globally competitive Europe should get more and better treatments to patients April 2026

Breaking the bottlenecks: How a more globally competitive Europe should get more and better treatments to patients April 2026 Rare diseases are individually uncommon but collectively touch the lives of around 30 million people across Europe, and more than 300 million worldwide. Yet around 95% of rare conditions still lack an authorised treatment, and even those with one face a series of bottlenecks: regulatory pathways that can take years, evidence standards that are difficult to meet with small patient populations, and reimbursement negotiations that vary dramatically by country. https://www.eurordis.org/breaking-the-bottlenecks-more-treatments-for-patients/