Epigenetic Modifiers as Therapeutic Targets GRIDS-2024 10th Anniversary CME Program

https://checkrare.com/learning/p-grids2024-session4-epigenetic-modifiers-as-therapeutic-targets/ Epigenetic Modifiers as Therapeutic Targets Katarina Trebušak Podkrajšek, PhD, Ali Beskok, PhD, Ying Sun, Professor, and Majdolen Istaiti (Joleen), B.Sc., MBA, analyze the development and delivery of ERT in neuronopathic Gaucher disease and explain the impact of the misfolding of the mutant glucocerebrosidase on the phenotypic heterogeneity of Gaucher disease