CLINICAL PERSPECTIVES +++ (3 videos)

CLINICAL PERSPECTIVES New Clinical Trial Testing On-Demand Use of Deucrictibant in Patients With Hereditary Angioedema https://checkrare.com/new-clinical-trial-testing-on-demand-use-of-deucrictibant-in-patients-with-hereditary-angioedema/ Peng Lu, MD, PhD, Chief Medical Officer at Pharvaris, and Wim Souverijns, PhD, Chief Commercial Officer at Pharvaris, discuss the RAPIDe-3 clinical trial of deucrictibant for patients with hereditary angioedema (HAE). ASMD Perspective Index: Diagnosing Niemann-Pick Disease https://checkrare.com/asmd-perspective-index-diagnosing-niemann-pick-disease/ John Taggart, Head of Communications at Niemann-Pick UK (NPUK), discusses the ASMD Perspective Index and its use in diagnosing Niemann-Pick disease. New Formulation of Berotralstat for Treatment of Pediatric Patients With Hereditary Angioedema https://checkrare.com/new-formulation-of-berotralstat-for-treatment-of-pediatric-patients-with-hereditary-angioedema/ Raffi Tachdjian, MD, Associate Clinical Professor of Medicine & Pediatrics, Division of Allergy & Clinical Immunology, University of California Los Angeles, discusses a new formulation of Orladeyo (berotralstat) for the treatment of pediatric patients with hereditary angioedema (HAE).