Drug Trials Snapshots: AQNEURSA (levacetylleucine)

AQNEURSA is a prescription medicine that is used to treat the neurological manifestations of Niemann-Pick disease, Type C (NPC) in adults and children who weigh 15 kg or more. https://www.fda.gov/drugs/drug-approvals-and-databases/drug-trials-snapshots-aqneursa