viernes, 25 de julio de 2025

For many Duchenne families, halt to gene therapy is heartbreak upon heartbreak A muscular dystrophy disease is devastating on its own, but a Sarepta treatment had offered hope

https://www.statnews.com/2025/07/24/duchenne-muscular-dystrophy-families-sarepta-elevydis/?utm_campaign=daily_recap&utm_medium=email&_hsenc=p2ANqtz--H-2H1QvT4N0uzTqBc_607GComNWYl6au7-16LDHbC_7UWd4uWjarZ5mm906sBrReRj8j_li75bgZvnIbVFFQhFcijTQ&_hsmi=372878121&utm_content=372878121&utm_source=hs_email

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