FDA Approves Gene Therapy (Waskyra) for Patients with Wiskott-Aldrich Syndrome +... ++

FDA Approves Gene Therapy (Waskyra) for Patients with Wiskott-Aldrich Syndrome The U.S. Food and Drug Administration (FDA) has… https://checkrare.com/ FDA NEWS 2025 Orphan Drugs: PDUFA Dates and FDA Approvals https://checkrare.com/2025-orphan-drugs-pdufa-dates-and-fda-approvals/ Rare diseases and orphan drugs are at the forefront of novel development and groundbreaking research. Almost half of all novel medications approved by the U.S. Food and Drug Administration (FDA) are orphan drugs. FDA Approves Obinutuzumab for Patients With Lupus Nephritis https://checkrare.com/fda-approves-obinutuzumab-for-patients-with-lupus-nephritis/ The U.S. Food and Drug Administration (FDA) has approved Gazyva/Gazyvaro (obinutuzumab) for the treatment of adults with active lupus nephritis who are receiving standard of care.