Hope for Niemann-Pick type C in FDA’s dual drug approval The FDA approved two new medications for Niemann-Pick disease type C that improve symptoms, showing the power of community advocacy.

https://www.drugdiscoverynews.com/hope-for-niemann-pick-type-c-in-fda-s-dual-drug-approval-16181?utm_campaign=DDN_Newsletter_Science%20Spotlight&utm_medium=email&_hsenc=p2ANqtz--_2xwP_9ViyDSiwkKvtkA3go6jGzYeUPh0H-3fERV-2lO8DWtXH17Hc9U3LHAeRrHiXmfWVPpL4x3hRSEUsU3jtRZ1Ew&_hsmi=339585239&utm_content=339585239&utm_source=hs_email