Effects of gene replacement therapy with resamirigene bilparvovec (AT132) on skeletal muscle pathology in X-linked myotubular myopathy: results from a substudy of the ASPIRO open-label clinical trial

https://www.thelancet.com/journals/ebiom/article/PIIS2352-3964(23)00460-7/fulltext?dgcid=hubspot_update_feature_updatealerts_ebiom&utm_campaign=update-ebiom&utm_medium=email&_hsmi=292241494&_hsenc=p2ANqtz-_cMBT4VZoVHwIIelUurnM6Rvg1ZZuryqJeIC6VP9eCetM9H5UY8WuSFq5XnpYtxI2t2t4NT8Kg9cYlqSK5B5x-5wYv2Q&utm_content=292190702&utm_source=hs_email