First-Ever Treatment For Rare Childhood Aging Disease Shows Improvement In All Trial Participants

First-Ever Treatment For Rare Childhood Aging Disease Shows Improvement In All Trial Participants

Boston Children's Hospital First-ever treatment for rare childhood aging disease shows improvement in all trial participants
Results of the first-ever clinical drug trial for children with Progeria, a rare, fatal “rapid-aging” disease, demonstrate the efficacy of a farnesyltransferase inhibitor (FTI), a drug originally developed to treat cancer.